Scholar Rock

At Scholar Rock, we are on a mission to discover, develop, and deliver therapies to improve people’s lives. We are a biopharmaceutical company combining bold science with a deep commitment to make a meaningful difference for people living with serious diseases. Founded on pioneering science from researchers at Harvard Medical School and Boston Children's Hospital, Scholar Rock is dedicated to enhancing the standard of care through innovative therapeutic approaches. Our unique scientific strategy allows us to selectively target growth factors, proteins that govern a wide range of biological functions, before they are activated. By essentially "shutting off the water supply before a faucet starts leaking," we aim to address diseases where these growth factors play a central role before they can cause significant harm.

Our commitment is not only to advance scientific knowledge but also to translate that knowledge into life-changing treatment options for patients who need them most. With a clinical pipeline that includes therapies for spinal muscular atrophy and other critical areas, such as immuno-oncology, we harness the power of growth factors in fundamentally different ways than traditional methods. This dedication to innovation, along with our collaboration with healthcare professionals and patient communities, positions Scholar Rock at the forefront of the biopharmaceutical industry. We believe in a future where our pioneering efforts create new possibilities for patients worldwide.