Ultragenyx Pharmaceutical Inc. develops innovative medicines for rare and ultrarare diseases, focusing on transformative therapies across multiple indications.
Alexion Pharmaceuticals, Inc. is a biopharmaceutical company dedicated to developing therapies for rare diseases.
Apellis Pharmaceuticals is a biopharmaceutical company specializing in targeted therapies for diseases impacted by the complement system.
Acadia Pharmaceuticals is dedicated to pioneering innovative therapies for neurological disorders, focusing on elevating the lives of patients through dedicated research and community support.
Axsome Therapeutics, Inc. is a commercial-stage biopharmaceutical company focused on developing and delivering novel therapies for central nervous system (CNS) disorders with limited treatment options. The company aims to transform the approach to treating CNS conditions by developing therapeutic options with innovative mechanisms of action.
Jazz Pharmaceuticals is a global biopharmaceutical company focused on developing innovative medicines to improve patients' lives.